Molecular Medicine Israel

CRISPR corrects β-thalassaemia

A common genetic blood disorder has been corrected in cultured stem cells by using a cutting-edge genome-editing technique.

The disorder β-thalassaemia is characterized by reduced levels of haemoglobin due to mutations in the gene for β-globin (HBB). Yuet Kan and his colleagues at the University of California, San Francisco, created induced…

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